Amyotrophic Lateral Sclerosis (ALS)
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Amyotrophic Lateral Sclerosis (ALS)
Amyotrophic Lateral Sclerosis (ALS) is a progressive motor neuron disease with limited treatment options historically. Recent breakthroughs include:
- Tofersen (Qalsody™) – antisense oligonucleotide for SOD1-mutated ALS
- Ongoing development of gene-silencing and neuroprotective strategies
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As a Nonprofit organization, we are deeply committed to raising awareness, providing patient support, and advocating for research for individuals living with various disease states.
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