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Rare Diseases

Acute Myeloid Leukemia (AML)

Acute myeloid leukemia (AML) is an aggressive and heterogeneous malignancy of the hematopoietic system characterized…

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Aplastic Anemia

Patient Education What is Aplastic Anemia? Aplastic anemia is a rare, but serious condition in which the bone marrow cannot…

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BPDCN

Blastic plasmacytoid dendritic cell neoplasm (BPDCN) is a rare and aggressive hematologic malignancy arising from precursor….

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Castleman's

Castleman disease is a lymphoproliferative disorder with a nondefinite etiology and can be classified into subtypes based on clinical…

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CLL/CML

Chronic lymphocytic leukemia (CLL) and chronic myeloid leukemia (CML) are hematologic malignancies characterized by the clonal….

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Cold Agglutinin Disease

Cold agglutinin disease (CAD) is a rare autoimmune disease that occurs when the body’s immune system attacks red blood cells…

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Diffuse Large B Cell Lymphoma

Diffuse large B-cell lymphoma (DLBCL) is a fast-growing, aggressive cancer that affects B cells, a type of white blood cell that produces antibodies..

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Hemolytic Disease of the Fetus and Newborn

Hemolytic disease of the fetus and newborn (HDFN), also known as hemolytic disease of the newborn (HDN) or erythroblastosis fetalis…

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Hemophagocytic Lymphohistiocytosis (HLH)

Hemophagocytic lymphohistiocytosis (HLH) is a rare, life-threatening immune deficiency disorder that occurs when certain white blood cells build…

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Hemophilia

Haemophilia, or hemophilia, is a mostly inherited genetic disorder that impairs the body’s ability to make blood clots, a process needed to stop bleeding…

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Immune Thrombocytopenia

Immune thrombocytopenic purpura (ITP) is a blood disorder. With this disease, you have a lower amount of platelets than normal in your blood….

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Mastocytosis

Mastocytosis is a rare disorder characterized by abnormal accumulation and activation of mast cells in the skin, bone marrow and internal organs…

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Myelodysplastic Syndrome

A myelodysplastic syndrome is one of a group of cancers in which immature blood cells in the bone marrow do not mature, and as a result, do not…

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Novel Cellular Therapies

Cellular therapies have revolutionized the treatment landscape for hematologic and solid malignancies, offering highly…

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Paroxysmal Nocturnal Hemoglobunuria

Paroxysmal nocturnal hemoglobinuria (PNH) is a rare, life-threatening blood disease that causes red blood cells to break down prematurely…

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Primary Central Nervous System Lymphoma

Primary central nervous system (CNS) lymphoma is an aggressive type of non-Hodgkin lymphoma that forms in the brain or spinal cord…..

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Rosai-Dorfman

Rosai-Dorfman disease (RDD) is a rare, benign condition that involves an overgrowth of white blood cells called histiocytes…

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Sickle Cell Disease

In sickle cell disease, red blood cells are misshaped, typically crescent- or “sickle”-shaped due to a gene mutation that affects…

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Systemic Mastocytosis

Systemic mastocytosis is an aggressive disorder characterized by the release of numerous vasoactive cell mediators due to excessive…

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